Webinar

Contents

Chair

Dr. Martin K. (Casey) Childers

Kinea Bio, Inc. United States

Speaker(s)

Prof. DAVID L. MACK

Department of Rehabilitation Medicine, University of Washington,  United States

Topic: DMD stem cell-derived cardiac and skeletal muscle research projects

Prof. De Wayne Townsend

Department of Integrative Biology and Physiology, University of Minnesota,  United States

Topic: Challenges and Opportunities in the Treatment of Dystrophic Cardiomyopathy

Dr. Yoshitsugu Aoki

Department of Molecular Therapy , National Institute of Neuroscience National Center of Neurology and Psychiatry, Japan

Topic: Development of Viltolarsen and Brogidirsen for the Treatment of Duchenne Muscular Dystrophy

Dr. Liubov V. Gushchina

Center for Gene Therapy , Nationwide Children’s Hospital,  United States

Topic: Therapeutic Development for Duchenne Muscular Dystrophy using Vectorized Exon-Skipping Approach

President Pat Furlong

Parent Project Muscular Dystrophy (PPMD),  United States

Topic: Advocate by Default

Programme
Programme
TimeChair / SpeakersTopic
PDTnext day
Japan
16:30 - 16:408:30-8:40Martin K. (Casey) ChildersWelcoming Address
16:40 - 17:008:40 – 9:00DAVID L. MACKDMD stem cell-derived cardiac and skeletal muscle research projects
17:00 - 17:209:00 – 9:20De Wayne TownsendChallenges and Opportunities in the Treatment of Dystrophic Cardiomyopathy
17:20 - 17:409:20 - 9:40Yoshitsugu AokiDevelopment of Viltolarsen and Brogidirsen for the Treatment of Duchenne Muscular Dystrophy
17:40 - 18:009:40 – 10:00Liubov V. GushchinaTherapeutic Development for Duchenne Muscular Dystrophy using Vectorized Exon-Skipping Approach
18:00 – 18:2010:00 – 10:20Pat FurlongAdvocate by Default
18:20 - 18:5010:20 - 10:50Martin K. (Casey) ChildersQ&A
18:50 - 19:0010:50 – 11:00Martin K. (Casey) ChildersConclusion
Rare Disease and Orphan Drugs Journal
ISSN 2771-2893 (Online)
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