Webinar
Contents
Chair
Dr. Martin K. (Casey) Childers
Speaker(s)
Prof. DAVID L. MACK
Department of Rehabilitation Medicine, University of Washington, United States
Topic: DMD stem cell-derived cardiac and skeletal muscle research projects
Prof. De Wayne Townsend
Department of Integrative Biology and Physiology, University of Minnesota, United States
Topic: Challenges and Opportunities in the Treatment of Dystrophic Cardiomyopathy
Dr. Yoshitsugu Aoki
Department of Molecular Therapy , National Institute of Neuroscience National Center of Neurology and Psychiatry, Japan
Topic: Development of Viltolarsen and Brogidirsen for the Treatment of Duchenne Muscular Dystrophy
Dr. Liubov V. Gushchina
Center for Gene Therapy , Nationwide Children’s Hospital, United States
Topic: Therapeutic Development for Duchenne Muscular Dystrophy using Vectorized Exon-Skipping Approach
Time | Chair / Speakers | Topic | |
PDT | next day Japan | ||
16:30 - 16:40 | 8:30-8:40 | Martin K. (Casey) Childers | Welcoming Address |
16:40 - 17:00 | 8:40 – 9:00 | DAVID L. MACK | DMD stem cell-derived cardiac and skeletal muscle research projects |
17:00 - 17:20 | 9:00 – 9:20 | De Wayne Townsend | Challenges and Opportunities in the Treatment of Dystrophic Cardiomyopathy |
17:20 - 17:40 | 9:20 - 9:40 | Yoshitsugu Aoki | Development of Viltolarsen and Brogidirsen for the Treatment of Duchenne Muscular Dystrophy |
17:40 - 18:00 | 9:40 – 10:00 | Liubov V. Gushchina | Therapeutic Development for Duchenne Muscular Dystrophy using Vectorized Exon-Skipping Approach |
18:00 – 18:20 | 10:00 – 10:20 | Pat Furlong | Advocate by Default |
18:20 - 18:50 | 10:20 - 10:50 | Martin K. (Casey) Childers | Q&A |
18:50 - 19:00 | 10:50 – 11:00 | Martin K. (Casey) Childers | Conclusion |
Presentation

RDODJ Introduction

Topic 1:DMD stem cell-derived cardiac and skeletal muscle research projects
Speaker:Prof. DAVID L. MACK

Topic2 : Challenges and Opportunities in the Treatment of Dystrophic Cardiomyopathy
Speaker:Prof. De Wayne Townsend

Topic 3:Development of Viltolarsen and Brogidirsen for the Treatment of Duchenne Muscular Dystrophy
Speaker:Dr. Yoshitsugu Aoki
