fig2
Figure 2. Diagram depicting DMD gene mutations associated with SAEs. Panels A, B, and C show the dystrophin structure, microdystrophin exon content of therapeutic transgenes, and patient mutations, respectively. From Bönnemann et al., 2023[31]. Republished under the Rights Link for Scientific Communications through the Copyright Clearance Center. SAEs: Severe adverse events; DMD: Duchenne muscular dystrophy.